aHUS Trials Watch 19- Iptacopan
FDA has approved the use of Iptacopan, brand name Fabhalta, for PNH. Two trials demonstrated that this Factor B complement inhibitor…
FDA has approved the use of Iptacopan, brand name Fabhalta, for PNH. Two trials demonstrated that this Factor B complement inhibitor…
Affordable treatment is a big issue for the majority of the world’s aHUS patients. Many live in countries that cannot afford…
To the best of Global Action’s knowledge there has not been a trial of subcutaneous Ravulizumab for use in the treatment…
For aHUS patients stopping eculizumab (or even Ravulizumab) treatment is an important but emotive issue. Having had the treatment when seriously…
Algorithms to diagnose aHUS apart from other syndromes of TMA exist, but why do these tools with problem solving steps seem under-utilized?
Two days ago an article appeared in BLOOD journal which was the result of a comprehensive analysis of data about patients…
Immunocompromisation is a hall mark of aHUS. For those who are predisposed to it and for those who have had it…
It is important that those using complement inhibitors remain alert to meningococcal infection a life threatening side effect of their use.…
About 4000 people around the world have had aHUS since the last aHUS awareness day. Many did not survive, they were…